HOW CAN WE HELP YOU TODAY?
- Sign up for a 2016 Challenge Event!
- Statement from Ionis & Biogen on the development of Ionis-SMNrx (Nusinersen)
- Ionis Pharmaceuticals completes enrollment for Phase 3 clinical trial of Ionis-SMNrx in children
- Roche announces new clinical trial for RG7916 in SMA
WHY SUPPORT THE SMA TRUST?Knowing that The SMA Trust is actively funding and driving research is both a comfort and a necessity. A cure for this devastating disease is clearly the ultimate goal but in the meantime, any research which leads to enhanced quality of life for anyone suffering from SMA must be supported, as any parent who has lost a child to SMA will understand. - Hannah Razzell
SMA Type I, 19 December 2011 – 21 September 2012